Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus-Reference-Cited by-同舟云学术

Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus

Published:2022-01 Issue:1 Volume:30 Page:223-237
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Vaidyanathan Sriram^ORCID,Baik Ron,Chen Lu,Bravo Dawn T.,Suarez Carlos J.,Abazari Shayda M.,Salahudeen Ameen A.,Dudek Amanda M.,Teran Christopher A.,Davis Timothy H.,Lee Ciaran M.,Bao Gang,Randell Scott H.,Artandi Steven E.,Wine Jeffrey J.,Kuo Calvin J.,Desai Tushar J.,Nayak Jayakar V.,Sellers Zachary M.,Porteus Matthew H.

Funder

National Institutes of Health

Cancer Prevention and Research Institute of Texas

Cystic Fibrosis Foundation

CIRM

Publisher

Elsevier BV

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