Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial

Author:

Heijerman Harry G M,McKone Edward F,Downey Damian G,Van Braeckel Eva,Rowe Steven M,Tullis Elizabeth,Mall Marcus A,Welter John J,Ramsey Bonnie W,McKee Charlotte M,Marigowda Gautham,Moskowitz Samuel M,Waltz David,Sosnay Patrick R,Simard Christopher,Ahluwalia Neil,Xuan Fengjuan,Zhang Yaohua,Taylor-Cousar Jennifer L,McCoy Karen S,McCoy Karen,Donaldson Scott,Walker Seth,Chmiel James,Rubenstein Ronald,Froh Deborah K.,Neuringer Isabel,Jain Manu,Moffett Kathryn,Taylor-Cousar Jennifer L.,Barnett Bruce,Mueller Gary,Flume Patrick,Livingston Floyd,Mehdi Nighat,Teneback Charlotte,Welter John,Jain Raksha,Kissner Dana,Patel Kapilkumar,Calimano Francisco J.,Johannes Jimmy,Daines Cori,Keens Thomas,Scher Herschel,Chittivelu Subramanyam,Reddivalam Sudhakar,Klingsberg Ross Carl,Johnson Larry G.,Verhulst Stijn,Macedo Patricia,Downey Damien,Connett Gary,Nash Edward,Withers Nicholas,Lee Timothy,Bakker Marleen,Heijerman Harry,Vermeulen Francois,Van Braeckel Eva,Knoop Christiane,De Wachter Elke,van der Meer Renske,Merkus Petrus,Majoor Christof

Funder

National Institutes of Health

Publisher

Elsevier BV

Subject

General Medicine

Reference27 articles.

1. Cystic fibrosis;Elborn;Lancet,2016

2. Altered chloride ion channel kinetics associated with the delta F508 cystic fibrosis mutation;Dalemans;Nature,1991

3. UK Cystic Fibrosis Registry. Annual data report 2017;Charman,2018

4. ECFSPR annual report 2017;Zolin,2019

5. Cystic Fibrosis Patient Registry. 2017 Annual data report;Marshall,2018

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