VX-445–Tezacaftor–Ivacaftor in Patients with Cystic Fibrosis and One or Two Phe508del Alleles

Author:

Keating Dominic1,Marigowda Gautham1,Burr Lucy1,Daines Cori1,Mall Marcus A.1,McKone Edward F.1,Ramsey Bonnie W.1,Rowe Steven M.1,Sass Laura A.1,Tullis Elizabeth1,McKee Charlotte M.1,Moskowitz Samuel M.1,Robertson Sarah1,Savage Jessica1,Simard Christopher1,Van Goor Fredrick1,Waltz David1,Xuan Fengjuan1,Young Tim1,Taylor-Cousar Jennifer L.1

Affiliation:

1. From Alfred Hospital, Melbourne, VIC (D.K.), and Mater Hospital, Brisbane, QLD (L.B.) — both in Australia; Vertex Pharmaceuticals, Boston (G.M., C.M.M., S.M.M., S.R., J.S., C.S., F.V.G., D.W., F.X., T.Y.); Banner University Medical Center, Tucson, AZ (C.D.); Universitätsmedizin Berlin and Berlin Institute of Health, Berlin, and the German Center for Lung Research, Giessen — both in Germany (M.A.M.); St. Vincent’s University Hospital and University College Dublin School of Medicine, Dublin (E.F.M.);...

Funder

Vertex Pharmaceuticals Incorporated

Publisher

Massachusetts Medical Society

Subject

General Medicine

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