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Enzyme replacement therapy for infantile-onset Pompe disease

Published:2017-11-20 Issue:12 Volume:2017 Page:
ISSN:1465-1858
Container-title:Cochrane Database of Systematic Reviews
language:en
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Author:

Chen Min¹²³⁴,Zhang Lingli¹²³⁴,Quan Shuyan¹²³⁴

Affiliation:

1. West China Second University Hospital, Sichuan University; Department of Pharmacy; No. 20, Section 4, Renmin South Road Chengdu China 610041

2. Sichuan University, Ministry of Education; Key Laboratory of Birth Defects and Related Diseases of Women and Children; Chengdu China

3. West China Second University Hospital, Sichuan University; Evidence-Based Pharmacy Center; Chengdu China

4. Sichuan University; Department of Obstetrics and Gynecology, West China Second University Hospital; Chengdu China

Publisher

Wiley

Subject

Pharmacology (medical)

Reference45 articles.

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2. Enzyme replacement therapy with recombinant human acid alpha glucosidase (rhGAA) in infantile onset Pompe disease (IOPD);Kishnani;Neuromuscular Disorders : NMD,2005

3. Kishnani PS Corzo D Leslie ND Gruskin D Van der Ploeg A Clancy JP Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease Pediatric Research 2009 329 35

4. Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease;Kishnani;Neurology,2007

5. Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease;Case;Neuromuscular Disorders,2015

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