Forskolin induced swelling (FIS) assay in intestinal organoids to guide eligibility for compassionate use treatment in a CF patient with a rare genotype-Reference-Cited by-同舟云学术

Forskolin induced swelling (FIS) assay in intestinal organoids to guide eligibility for compassionate use treatment in a CF patient with a rare genotype

Published:2022-03 Issue:2 Volume:21 Page:254-257
ISSN:1569-1993
Container-title:Journal of Cystic Fibrosis
language:en
Short-container-title:Journal of Cystic Fibrosis

Author:

Aalbers B.L.,Brunsveld J.E.,van der Ent C.K.,van den Eijnden J.C.,Beekman J.M.,Heijerman H.G.M.

Publisher

Elsevier BV

Subject

Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health

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2. Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial;Heijerman;Lancet,2019

3. Diagnosis of cystic fibrosis: consensus guidelines from the cystic fibrosis foundation;Farrell;J Pediatr,2017

4. A functional CFTR assay using primary cystic fibrosis intestinal organoids;Dekkers;Nat Med,2013

5. Characterizing responses to CFTR-modulating drugs using rectal organoids derived from subjects with cystic fibrosis;Dekkers;Sci Transl Med,2016

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