Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2-Reference-Cited by-同舟云学术

Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2

Published:2013-06 Issue:6 Volume:120 Page:1283-1291
ISSN:0161-6420
Container-title:Ophthalmology
language:en
Short-container-title:Ophthalmology

Author:

Testa Francesco,Maguire Albert M.,Rossi Settimio,Pierce Eric A.,Melillo Paolo,Marshall Kathleen,Banfi Sandro,Surace Enrico M.,Sun Junwei,Acerra Carmela,Wright J. Fraser,Wellman Jennifer,High Katherine A.,Auricchio Alberto,Bennett Jean,Simonelli Francesca

Publisher

Elsevier BV

Subject

Ophthalmology

Reference28 articles.

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3. Effect of gene therapy on visual function in Leber's congenital amaurosis;Bainbridge;N Engl J Med,2008

4. Visual acuity in patients with Leber's congenital amaurosis and early childhood-onset retinitis pigmentosa;Walia;Ophthalmology,2010

5. Treatment of Leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial;Hauswirth;Hum Gene Ther,2008

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