1. Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials;Maguire;Ophthalmology,2019
2. Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial;Russell;Lancet,2017
3. Macular Fold Complicating a Subretinal Injection of Voretigene Neparvovec;Ducloyer;Ophthalmol Retina,2020
4. Short term morphological rescue of the fovea after gene therapy with voretigene neparvovec;Kortum;Acta Ophthalmol,2021
5. Visual Acuity, Retinal Morphology, and Patients' Perceptions after Voretigene Neparvovec-rzyl for RPE65-Associated Retinal Disease;Sengillo;Ophthalmol Retina,2021