Iduronate-2-sulfatase transport vehicle rescues behavioral and skeletal phenotypes in a mouse model of Hunter syndrome-Reference-Cited by-同舟云学术

Iduronate-2-sulfatase transport vehicle rescues behavioral and skeletal phenotypes in a mouse model of Hunter syndrome

Published:2021-10-08 Issue:19 Volume:6 Page:
ISSN:2379-3708
Container-title:JCI Insight
language:en
Short-container-title:

Author:

Arguello Annie,Meisner René,Thomsen Elliot R.,Nguyen Hoang N.^ORCID,Ravi Ritesh^ORCID,Simms Jeffrey,Lo Iris,Speckart Jessica,Holtzman Julia,Gill Thomas M.,Chan Darren^ORCID,Cheng Yuhsiang,Chiu Chi-Lu,Dugas Jason C.,Fang Meng,Lopez Isabel A.,Solanoy Hilda,Tsogtbaatar Buyankhishig,Zhu Yuda^ORCID,Bhalla Akhil,Henne Kirk R.,Henry Anastasia G.^ORCID,Delucchi Anthony,Costanzo Simona,Harris Jeffrey M.,Diaz Dolores^ORCID,Scearce-Levie Kimberly,Sanchez Pascal E.^ORCID

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Link

https://insight.jci.org/articles/view/145445/files/pdf

Reference44 articles.

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3. Recognition and Diagnosis of Mucopolysaccharidosis II (Hunter Syndrome)

4. Brain pathology in mucopolysaccharidoses (MPS) patients with neurological forms;Viana;J Clin Med,2020

5. Mucopolysaccharidosis Type II: One Hundred Years of Research, Diagnosis, and Treatment

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