Gene therapy for leukodystrophies
Author:
Publisher
Oxford University Press (OUP)
Subject
Genetics (clinical),Genetics,Molecular Biology,General Medicine
Link
http://academic.oup.com/hmg/article-pdf/20/R1/R42/1763697/ddr142.pdf
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1. Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters
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3. Molecular Basis of Different Forms of Metachromatic Leukodystrophy
4. Cloning and expression cDNA encoding human galactocerebrosidase, the enzyme deficient in globoid cell leukodystrophy
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