1. Gene Therapeutics Research Institute, Cedars-Sinai Medical Center, Los Angeles, CA 90048.
2. Molecular Medicine and Gene Therapy Unit, Department of Medicine, University of Manchester, Manchester M13 9PL, UK.
3. Telethon Institute for Gene Therapy, Vita-Salute San Raffaele University Medical School, University of Milan, Milan 20132, Italy.
4. Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, CA 90095.