Silencing Mutant Huntingtin by Adeno-Associated Virus-Mediated RNA Interference Ameliorates Disease Manifestations in the YAC128 Mouse Model of Huntington's Disease
Author:
Affiliation:
1. Genzyme (a Sanofi Company), Framingham, MA 01701.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2013.200
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5. Huntingtin aggregation and toxicity in Huntington's disease
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