Lentiviral Gene Therapy for Familial Hemophagocytic Lymphohistiocytosis Type 3, Caused by UNC13D Genetic Defects-Reference-Cited by-同舟云学术

Lentiviral Gene Therapy for Familial Hemophagocytic Lymphohistiocytosis Type 3, Caused by UNC13D Genetic Defects

Published:2020-06-01 Issue:11-12 Volume:31 Page:626-638
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Takushi Sarah E.¹²³,Paik Na Yoon²³,Fedanov Andrew²³,Prince Chengyu²³,Doering Christopher B.²³⁴,Spencer H. Trent²³⁴,Chandrakasan Shanmuganathan²³⁵

Affiliation:

1. Department of Immunology and Molecular Pathogenesis, Graduate Division of Biological and Biomedical Sciences, Laney Graduate School, Emory University, Atlanta, Georgia, USA.

2. Cell and Gene Therapy Program, Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Atlanta, Georgia, USA.

3. Department of Pediatrics, Emory University, Atlanta, Georgia, USA.

4. Department of Molecular and Systems Pharmacology, Graduate Division of Biological and Biomedical Sciences, Emory University School of Medicine, Atlanta, Georgia, USA.

5. Bone Marrow Transplant Program, Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Atlanta, Georgia, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2019.329

Reference67 articles.

1. HLH-2004: Diagnostic and therapeutic guidelines for hemophagocytic lymphohistiocytosis

2. Early B cell changes predict autoimmunity following combination immune checkpoint blockade

3. Hemophagocytic lymphohistiocytosis (HLH) and related disorders

4. Proliferation through activation: hemophagocytic lymphohistiocytosis in hematologic malignancy

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