Gene Therapy Fully Restores Vision to the All-Cone Nrl−/−Gucy2e−/− Mouse Model of Leber Congenital Amaurosis-1-Reference-Cited by-同舟云学术

Gene Therapy Fully Restores Vision to the All-Cone Nrl−/−Gucy2e−/− Mouse Model of Leber Congenital Amaurosis-1

Published:2015-09 Issue:9 Volume:26 Page:575-592
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Boye Sanford L.¹,Peterson James J.¹,Choudhury Shreyasi¹,Min Seok Hong¹,Ruan Qing¹,McCullough K. Tyler¹,Zhang Zhonghong¹,Olshevskaya Elena V.²,Peshenko Igor V.²,Hauswirth William W.¹,Ding Xi-Qin³,Dizhoor Alexander M.²,Boye Shannon E.¹

Affiliation:

1. Department of Ophthalmology, College of Medicine, University of Florida, Gainesville, Florida.

2. Department of Basic Sciences Research, Salus University, Elkins Park, Pennsylvania.

3. Department of Cell Biology, College of Medicine, University of Oklahoma, Oklahoma City, Oklahoma.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2015.053

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