Gene Therapy for Hemophilia and Duchenne Muscular Dystrophy in China
Author:
Affiliation:
1. School of Life Sciences, Central South University, Changsha, China.
2. Hunan Jiahui Genetics Hospital, Changsha, China.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2017.213
Reference57 articles.
1. Current Progress in Therapeutic Gene Editing for Monogenic Diseases
2. Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B
3. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B
4. Worldwide Epidemiology of Neutralizing Antibodies to Adeno‐Associated Viruses
Cited by 5 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Therapeutic Application of Extracellular Vesicles-Capsulated Adeno-Associated Virus Vector via nSMase2/Smpd3, Satellite, and Immune Cells in Duchenne Muscular Dystrophy;International Journal of Molecular Sciences;2022-01-28
2. Applications and developments of gene therapy drug delivery systems for genetic diseases;Asian Journal of Pharmaceutical Sciences;2021-11
3. CRISPR/Cas9-Mediated in vivo Genetic Correction in a Mouse Model of Hemophilia A;Frontiers in Cell and Developmental Biology;2021-08-16
4. Natural products, PGC-1 , and Duchenne muscular dystrophy;Acta Pharmaceutica Sinica B;2020-05
5. Emerging therapies for haemophilia - Global perspective;Haemophilia;2018-05
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3