A Sequel to the Eteplirsen Saga: Eteplirsen Is Approved in the United States but Was Not Approved in Europe
Author:
Affiliation:
1. Department of Human Genetics, Leiden University Medical Center, Leiden, the Netherlands.
2. Department of Child Neurology, University Hospitals Leuven, Leuven, Belgium.
Publisher
Mary Ann Liebert Inc
Subject
Drug Discovery,Genetics,Molecular Biology,Molecular Medicine,Biochemistry
Link
https://www.liebertpub.com/doi/pdf/10.1089/nat.2018.0756
Reference9 articles.
1. FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga
2. Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations
3. The TREAT-NMD DMD Global Database: Analysis of More than 7,000 Duchenne Muscular Dystrophy Mutations
4. Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy
5. Ambulatory capacity and disease progression as measured by the 6-minute-walk-distance in Duchenne muscular dystrophy subjects on daily corticosteroids
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