Efficacy and Safety of Elamipretide in Individuals With Primary Mitochondrial Myopathy

Author:

Karaa Amel1ORCID,Bertini Enrico1ORCID,Carelli Valerio1,Cohen Bruce H.1,Enns Gregory M.1,Falk Marni J.1,Goldstein Amy1,Gorman Gráinne Siobhan1ORCID,Haas Richard1,Hirano Michio1ORCID,Klopstock Thomas1,Koenig Mary Kay1,Kornblum Cornelia1,Lamperti Costanza1,Lehman Anna1,Longo Nicola1,Molnar Maria Judit1,Parikh Sumit1,Phan Han1,Pitceathly Robert D.S.1ORCID,Saneto Russell1,Scaglia Fernando1ORCID,Servidei Serenella1,Tarnopolsky Mark1,Toscano Antonio1,Van Hove Johan L.K.1,Vissing John1ORCID,Vockley Jerry1ORCID,Finman Jeffrey S.1,Brown David A.1ORCID,Shiffer James A.1,Mancuso Michelango1ORCID,Lucia Valentino Maria,Alessandro Primiano Guido,Cristina Sancricca,Zoltan Grosz,Bathori Györgyi,Daria Diodato,Gessica Vasco,Claudia Soler-Alfonso,Ali Abdullhameed May,Michael G Hanna,Enrico Bugiardini,Olivia V Poole,Fran Kendall,A Larson,Ajantha Nithi,Kristin Engelstad,Andre Mattman,Michelle Mezei,Alamut T Bischoff,Boriana Büchner,Florentine Radelfahr,Claudia Stendel,Claudia B Catarino,Elizabeth Tonni Hilary,Tait Rossman Ian,Marie Cole Kristin,Christina Victorio Maria,Vincenzo Montano,Gabriele Siciliano,Olimpia Musumeci,Alessina Catania, ,

Affiliation:

1. From the Massachusetts General Hospital (A.K.), Harvard Medical School Boston; Neuromuscular Unit (E.B.), Bambino Gesù Ospedale Pediatrico, IRCCS, Rome; IRCCS Istituto delle Scienze Neurologiche di Bologna (V.C.), Programma di Neurogenetica; Department of Biomedical and Neuromotor Sciences (V.C.), University of Bologna, Italy; Rebecca D. Considine Research Institute (B.H.C.), Akron Children's Hospital, OH; Stanford University School of Medicine (G.M.E.), CA; Mitochondrial Medicine Frontier Program ...

Publisher

Ovid Technologies (Wolters Kluwer Health)

Subject

Neurology (clinical)

Reference41 articles.

1. NORD physician guide to mitochondrial myopathies (MM);Mancuso M;Nat Org Rare Disord.,2016

2. International Workshop:

3. Mitochondrial medicine in the omics era

4. Diagnosis and treatment of mitochondrial myopathies

5. Exercise testing as a diagnostic entity in mitochondrial myopathies;Tarnopolsky M;Mitochondrion,2004

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