P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database

Author:

Hansen Bettina,Valcheva Velichka,Yu Qifeng,Wessel Daan BE van,Thompson Richard J,Gonzales Emmanuel,Jankowska Irena,Sokal Etienne,Grammatikopoulos Tassos,Kadaristiana Agustina,Jacquemin Emmanuel,Spraul Anne,Lipiński Patryk,Czubkowski Piotr,Rock Nathalie,Shagrani Mohammad,Kumar Kishwer,Alkuraya Fowzan,Sateesh Meddirevula,Broering Dieter,Nicastro Emanuele,Kelly Deirdre A,Nebbia Gabriella,Arnell Henrik,Fischler Björn,Serranti Daniele,Arikan Cigdem,Polat Esra,Debray Dominique,Lacaille Florence,Goncalves Cristina,Hierro Loreto,Bartolo Gema Muñoz,Mozer-Glassberg Yael,Azaz Amer,Brecelj Jernej,Dezsőfi Antal,Calvo Pier Luigi,Grabhorn Enke,Sturm Ekkehard,Woerd Wendy L van der,Kamath Binita M,Wang Jian-She,Li Liting,Durmaz Özlem,Onal Zerrin,Felzen Antonia,Nomden Mark,Sonajalg Jaak,Stein Philip,Ni Quanhong,Clemson Christine,Mattsson Jan P,Verkade Henkjan J

Publisher

BMJ Publishing Group Ltd and British Society of Gastroenterology

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