1. Division of Hematology/Oncology, Department of Medicine, University of California San Diego, San Diego, CA;
2. Division of Hematology/Oncology, Department of Medicine, Hemophilia Treatment Center, University of California Davis, Sacramento, CA;
3. Careggi University Hospital, Florence, Italy;
4. Division of Hematology/Oncology, Department of Medicine, University of North Carolina, Chapel Hill, NC;
5. The Hemophilia Center, Oregon Health & Science University, Portland, OR;
6. Erasmus University Medical Center, Rotterdam, The Netherlands;
7. Department of Hemostaseology and Hemophilia Center, Medical Clinic 2, Institute of Transfusion Medicine, University Hospital Frankfurt, Frankfurt, Germany;
8. uniQure Inc, Lexington, MA; and
9. Department of Pediatrics and Pathology, University of Michigan, Ann Arbor, MI