1. Centre for Cardiovascular Sciences, School of Clinical and Experimental Medicine, College of Medical and Dental Sciences, University of Birmingham, Birmingham, United Kingdom;
2. Medical Research Council, Laboratory for Molecular Cell Biology, University College London, London, United Kingdom;
3. University College London Institute of Child Health, Gene Therapy Laboratory, London, United Kingdom;
4. Laboratory of Immunogenetics of Pediatric Autoimmune Diseases, Paris, France;
5. Department of General Pediatrics, University Children’s Hospital, Muenster, Germany;
6. Department of Pediatric Nephrology, University Hospital Vall d’Hebron, Barcelona, Spain;
7. School of Cellular and Molecular Medicine, University of Bristol, Bristol, United Kingdom; and
8. Inherited Metabolic Diseases, Great Ormond Street Hospital, London, United Kingdom