1. From the Cell and Gene Therapy Program, St Jude Children's Research Hospital, Memphis, TN; the Center for Gene Therapy, MCP-Hahnemann Medical School, Philadelphia, PA; the Department of Pediatrics and Obstetrics/Gynecology, Wayne State University, Detroit, MI; the Department of Internal Medicine, Mayo Clinic, Rochester, NY; the Department of Pediatrics, University of Minnesota, Minneapolis, MN; and the Department of Human Genetics, MCP Hahnemann, Pittsburgh, PA.