1. Center for Genetic Medicine Research, Children’s Research Institute, Children’s National Hospital, Washington, DC, USA
2. Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, DC, USA
3. School of Pharmacy and Pharmaceutical Sciences, Binghamton University, Binghamton, NY, USA
4. The Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK
5. National Institute for Health Research, Great Ormond Street Institute of Child Health Biomedical Research Centre, University College London, London, UK