Author:
Pillay S.,Meyer N. L.,Puschnik A. S.,Davulcu O.,Diep J.,Ishikawa Y.,Jae L. T.,Wosen J. E.,Nagamine C. M.,Chapman M. S.,Carette J. E.
Publisher
Springer Science and Business Media LLC
Reference32 articles.
1. Kotterman, M. A. & Schaffer, D. V. Engineering adeno-associated viruses for clinical gene therapy. Nature Rev. Genet. 15, 445–451 (2014)
2. Nathwani, A. C. et al. Adenovirus-associated virus vector-mediated gene transfer in hemophilia B. N. Engl. J. Med . 365, 2357–2365 (2011)
3. Gaudet, D., Methot, J. & Kastelein, J. Gene therapy for lipoprotein lipase deficiency. Curr. Opin. Lipidol. 23, 310–320 (2012)
4. Lisowski, L. et al. Selection and evaluation of clinically relevant AAV variants in a xenograft liver model. Nature 506, 382–386 (2014)
5. Summerford, C. & Samulski, R. J. Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J. Virol. 72, 1438–1445 (1998)