Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector-Reference-Cited by-同舟云学术

Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector

Published:2016-04 Issue:4 Volume:24 Page:726-735
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Choudhury Sourav R,Harris Anne F,Cabral Damien J,Keeler Allison M,Sapp Ellen,Ferreira Jennifer S,Gray-Edwards Heather L,Johnson Jacob A,Johnson Aime K,Su Qin,Stoica Lorelei,DiFiglia Marian,Aronin Neil,Martin Douglas R,Gao Guangping,Sena-Esteves Miguel

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Eight years of clinical improvement in MPTP-lesioned primates after gene therapy with AAV2-hAADC;Hadaczek;Mol Ther,2010

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