In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model-Reference-Cited by-同舟云学术

In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model

Published:2022-12-01 Issue: Volume: Page:
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Chen Yi A.,Kankel Mark W.,Hana Sam^ORCID,Lau Shukkwan Kelly,Zavodszky Maria I.,McKissick Olivia^ORCID,Mastrangelo Nicole,Dion Jessica,Wang Bin,Ferretti Daniel,Koske David,Lehman Sydney,Koszka Kathryn,McLaughlin Helen,Liu Mei,Marshall Eric,Fabian Attila J.,Cullen Patrick,Marsh Galina,Hamann Stefan^ORCID,Craft Michael,Sebalusky Jennifer,Arnold H. Moore,Driscoll Rachelle,Sheehy Adam^ORCID,Luo Yi,Manca Sonia^ORCID,Carlile Thomas,Sun Chao,Sigrist Kirsten^ORCID,McCampbell Alexander,Henderson Christopher E.,Lo Shih-Ching^ORCID

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.nature.com/articles/s41434-022-00375-w.pdf

Reference65 articles.

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