1. Department of Internal Medicine, Referral Center for Lysosomal Diseases, Beaujon Hospital, AP-HP, Université Paris Cité, 92110 Clichy, France
2. Department of Biological and Clinical Hematology, Estaing Hospital, CHU Clermont-Ferrand, 63000 Clermont-Ferrand, France
3. Department of Hematology, Saint Vincent de Paul Hospital, GHICL, 59000 Lille, France
4. CEN Biotech, 21000 Dijon, France
5. Clario Inc. (Formerly Bioclinica, Inc.), 69006 Lyon, France
6. Clario Inc. (Formerly Bioclinica, Inc.), 20355 Hamburg, Germany
7. Takeda France SAS, 75116 Paris, France