Adeno‐associated virus 8‐mediated gene therapy for choroideremia: preclinical studies in in vitro and in vivo models-Reference-Cited by-同舟云学术

Adeno‐associated virus 8‐mediated gene therapy for choroideremia: preclinical studies in in vitro and in vivo models

Published:2014-05 Issue:5-6 Volume:16 Page:122-130
ISSN:1099-498X
Container-title:The Journal of Gene Medicine
language:en
Short-container-title:J Gene Med

Author:

Black Aaron¹,Vasireddy Vidyullatha¹,Chung Daniel C.¹,Maguire Albert M.¹,Gaddameedi Rajashekhar¹,Tolmachova Tania²,Seabra Miguel²,Bennett Jean¹

Affiliation:

1. F.M. Kirby Center for Molecular Ophthalmology and Center for Advanced Retinal and Ophthalmic Therapeutics Scheie Eye Institute, University of Pennsylvania School of Medicine Philadelphia PA USA

2. Molecular Medicine Imperial College London London UK

Funder

Foundation Fighting Blindness

Choroideremia Research Foundation

F.M. Kirby Foundation

Mackall Foundation Trust

Penn Genome Frontiers Institute

Research to Prevent Blindness

Publisher

Wiley

Subject

Genetics (clinical),Drug Discovery,Genetics,Molecular Biology,Molecular Medicine

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/jgm.2768

Reference42 articles.

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2. A practical diagnostic test for choroideremia

3. Rab escort protein-1 is a multifunctional protein that accompanies newly prenylated rab proteins to their target membranes.

4. Prenylation of Rab GTPases: molecular mechanisms and involvement in genetic disease

5. Multiple Factors Contribute to Inefficient Prenylation of Rab27a in Rab Prenylation Diseases

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