1. Department of PediatricsOhio State UniversityColumbusOhio
2. Center for Gene Therapy Nationwide Children's HospitalColumbusOhio
3. Department of Pharmacy Systems, Outcomes, and PolicyUniversity of IllinoisChicagoIllinois
4. AveXis, Inc.BannockburnIllinois
5. Department of NeurologyOhio State UniversityColumbusOhio