Long‐term safety and efficacy of eculizumab in generalized myasthenia gravis

Author:

Muppidi Srikanth1,Utsugisawa Kimiaki2,Benatar Michael3,Murai Hiroyuki4,Barohn Richard J.5,Illa Isabel67,Jacob Saiju8,Vissing John9,Burns Ted M.10,Kissel John T.11,Nowak Richard J.12,Andersen Henning13,Casasnovas Carlos714,Bleecker Jan L.15,Vu Tuan H.16,Mantegazza Renato17,O'Brien Fanny L.18,Wang Jing Jing18,Fujita Kenji P.18,Howard James F.19ORCID,Mazia Claudio Gabriel,Wilken Miguel,Barroso Fabio,Saba Juliet,Rugiero Marcelo,Bettini Mariela,Chaves Marcelo,Vidal Gonzalo,Garcia Alejandra Dalila,Van den Abeele Guy,de Koning Kathy,De Mey Katrien,Mercelis Rudy,Mahieu Délphine,Wagemaekers Linda,Van Damme Philip,Depreitere Annelies,Schotte Caroline,Smetcoren Charlotte,Stevens Olivier,Van Daele Sien,Vandenbussche Nicolas,Vanhee Annelies,Verjans Sarah,Vynckier Jan,D'Hondt Ann,Tilkin Petra,Alves de Siqueira Carvalho Alzira,Dias Brockhausen Igor,Feder David,Ambrosio Daniel,César Pamela,Melo Ana Paula,Martins Ribeiro Renata,Rocha Rosana,Bezerra Rosa Bruno,Veiga Thabata,da Silva Luiz Augusto,Santos Engel Murilo,Gonçalves Geraldo Jordana,Ananias Morita Maria da Penha,Nogueira Coelho Erica,Paiva Gabriel,Pozo Marina,Prando Natalia,Martineli Torres Debora Dada,Butinhao Cristiani Fernanda,Duran Gustavo,Gomes da Silva Tamires Cristina,Otavio Maia Gonçalves Luiz,Pazetto Lucas Eduardo,Fialho Tomás Augusto Suriane,Renata Cubas Volpe Luciana,Souza Duca Luciana,Gheller Friedrich Maurício André,Guerreiro Alexandre,Mohr Henrique,Pereira Martins Maurer,da Cruz Pacheco Daiane,Ferreira Luciana,Macagnan Ana Paula,Pinto Graziela,Santos Aline de Cassia,Souza Bulle Oliveira Acary,Amaral Andrade Ana Carolina,Annes Marcelo,Duarte Silva Liene,Cavalcante Lino Valeria,Pinto Wladimir,Assis Natália,Carrara Fernanda,Miranda Carolina,Souza Iandra,Fernandes Patricia,Siddiqi Zaeem,Phan Cecile,Narayan Jeffrey,Blackmore Derrick,Mallon Ashley,Roderus Rikki,Watt Elizabeth,Vohanka Stanislav,Bednarik Josef,Chmelikova Magda,Cierny Marek,Toncrova Stanislava,Junkerova Jana,Kurkova Barbora,Reguliova Katarina,Zapletalova Olga,Pitha Jiri,Novakova Iveta,Tyblova Michaela,Jurajdova Ivana,Wolfova Marcela,Harbo Thomas,Vinge Lotte,Krogh Susanne,Mogensen Anita,Højgaard Joan,Witting Nanna,Ostergaard Autzen Anne,Pedersen Jane,Eralinna Juha-Pekka,Laaksonen Mikko,Oksaranta Olli,Harrison Tuula,Eriksson Jaana,Rozsa Csilla,Horvath Melinda,Lovas Gabor,Matolcsi Judit,Szabo Gyorgyi,Jakab Gedeonne,Szabadosne Brigitta,Vecsei Laszlo,Dezsi Livia,Varga Edina,Konyane Monika,Antonini Giovanni,Di Pasquale Antonella,Garibaldi Matteo,Morino Stefania,Troili Fernanda,Fionda Laura,Filla Allessandro,Costabile Teresa,Marano Enrico,Saccà Francesco,Fasanaro Angiola,Marsili Angela,Puorro Giorgia,Antozzi Carlo,Bonanno Silvia,Camera Giorgia,Locatelli Alberta,Maggi Lorenzo,Pasanisi Maria,Campanella Angela,Evoli Amelia,Alboini Paolo Emilio,D'Amato Valentina,Iorio Raffaele,Inghilleri Maurizio,Fionda Laura,Frasca Vittorio,Giacomelli Elena,Gori Maria,Lopergolo Diego,Onesti Emanuela,Frasca Vittorio,Gabriele Maria,Uzawa Akiyuki,Kanai Tetsuya,Kawaguchi Naoki,Mori Masahiro,Kaneko Yoko,Kanzaki Akiko,Kobayashi Eri,Masaki Katsuhisa,Matsuse Dai,Matsushita Takuya,Uehara Taira,Shimpo Misa,Jingu Maki,Kikutake Keiko,Nakamura Yumiko,Sano Yoshiko,Nagane Yuriko,Kamegamori Ikuko,Tsuda Tomoko,Fujii Yuko,Futono Kazumi,Ozawa Yukiko,Mizugami Aya,Saito Yuka,Suzuki Hidekazu,Morikawa Miyuki,Samukawa Makoto,Kamakura Sachiko,Miyawaki Eriko,Shiraishi Hirokazu,Mitazaki Teiichiro,Motomura Masakatsu,Mukaino Akihiro,Yoshimura Shunsuke,Asada Shizuka,Yoshida Seiko,Amamoto Shoko,Kobashikawa Tomomi,Koga Megumi,Maeda Yasuko,Takada Kazumi,Takada Mihoko,Tsurumaru Masako,Yamashita Yumi,Suzuki Yasushi,Akiyama Tetsuya,Narikawa Koichi,Tano Ohito,Tsukita Kenichi,Kurihara Rikako,Meguro Fumie,Fukuda Yusuke,Sato Miwako,Okumura Meinoshin,Funaka Soichiro,Kawamura Tomohiro,Makamori Masayuki,Takahashi Masanori,Taichi Namie,Hasuike Tomoya,Higuchi Eriko,Kobayashi Hisako,Osakada Kaori,Imai Tomihiro,Tsuda Emiko,Shimohama Shun,Hayashi Takashi,Hisahara Shin,Kawamata Jun,Murahara Takashi,Saitoh Masaki,Suzuki Shuichiro,Yamamoto Daisuke,Ishiyama Yoko,Ishiyama Naoko,Noshiro Mayuko,Takeyama Rumi,Uwasa Kaori,Yasuda Ikuko,van der Kooi Anneke,de Visser Marianne,Gibson Tamar,Kim Byung-Jo,Lee Chang Nyoung,Koo Yong Seo,Seok Hung Youl,Kang Hoo Nam,Ra HyeJin,Kim Byoung Joon,Cho Eun Bin,Choi MiSong,Lee HyeLim,Min Ju-Hong,Seok Jinmyoung,Lee JiEun,Koh Da Yoon,Kwon JuYoung,Park SangAe,Choi Eun Hwa,Hong Yoon-Ho,Ahn So-Hyun,Koo Dae Lim,Lim Jae-Sung,Shin Chae Won,Hwang Ji Ye,Kim Miri,Kim Seung Min,Jeong Ha-Neul,Jung JinWoo,Kim Yool-hee,Lee Hyung Seok,Shin Ha Young,Hwang Eun Bi,Shin Miju,Alberti Aguilo Maria Antonia,Homedes-Pedret Christian,Julia Palacios Natalia,Diez Porras Laura,Velez Santamaria Valentina,Lazaro Ana,Diez Tejedor Exuperio,Gomez Salcedo Pilar,Fernandez-Fournier Mireya,Lopez Ruiz Pedro,Rodriguez de Rivera Francisco Javier,Sastre Maria,Gamez Josep,Sune Pilar,Salvado Maria,Gili Gisela,Mazuela Gonzalo,Cortes Vicente Elena,Diaz-Manera Jordi,Querol Gutierrez Luis Antonio,Rojas Garcia Ricardo,Vidal Nuria,Arribas-Ibar Elisabet,Piehl Fredrik,Hietala Albert,Bjarbo Lena,Sengun Ihsan,Meherremova Arzu,Ozcelik Pinar,Balkan Bengu,Tuga Celal,Ugur Muzeyyen,Erdem-Ozdamar Sevim,Bekircan‐Kurt Can Ebru,Acar Nazire Pinar,Yilmaz Ezgi,Caliskan Yagmur,Orsel Gulsah,Efendi Husnu,Aydinlik Seda,Cavus Hakan,Kutlu Ayse,Becerikli Gulsar,Semiz Cansu,Tun Ozlem,Terzi Murat,Dogan Baki,Onar Musa Kazim,Sen Sedat,Kirbas Cavdar Tugce,Veske Adife,Norwood Fiona,Dimitriou Aikaterini,Gollogly Jakit,Mahdi-Rogers Mohamed,Seddigh Arshira,Sokratous Giannis,Maier Gal,Sohail Faisal,Sadalage Girija,Torane Pravin,Brown Claire,Shah Amna,Sathasivam Sivakumar,Arndt Heike,Davies Debbie,Watling Dave,Amato Anthony,Cochrane Thomas,Salajegheh Mohammed,Roe Kristen,Amato Katherine,Toska Shirli,Wolfe Gil,Silvestri Nicholas,Patrick Kara,Zakalik Karen,Katz Jonathan,Miller Robert,Engel Marguerite,Forshew Dallas,Bravver Elena,Brooks Benjamin,Plevka Sarah,Burdette Maryanne,Cunningham Scott,Sanjak Mohammad,Kramer Megan,Nemeth Joanne,Schommer Clara,Tierney Scott,Juel Vern,Guptill Jeffrey,Hobson-Webb Lisa,Massey Janice,Beck Kate,Carnes Donna,Loor John,Anderson Amanda,Pascuzzi Robert,Bodkin Cynthia,Kincaid John,Snook Riley,Guingrich Sandra,Micheels Angela,Chaudhry Vinay,Corse Andrea,Mosmiller Betsy,Kelley Andrea,Ho Doreen,Srinivasan Jayashri,Vytopil Michal,Jara Jordan,Ventura Nicholas,Scala Stephanie,Carter Cynthia,Donahue Craig,Herbert Carol,Weiner Elaine,Alam Sharmeen,McKinnon Jonathan,Haar Laura,McKinnon Naya,Alcon Karan,McKenna Kaitlyn,Sattar Nadia,Daniels Kevin,Jeffery Dennis,Freimer Miriam,Hoyle Joseph Chad,Agriesti Julie,Chelnick Sharon,Mezache Louisa,Pineda Colleen,Muharrem Filiz,Karam Chafic,Khoury Julie,Marburger Tessa,Kaur Harpreet,Dimitrova Diana,Gilchrist James,Agrawal Brajesh,Elsayed Mona,Kohlrus Stephanie,Andoin Angela,Darnell Taylor,Golden Laura,Lokaitis Barbara,Seelback Jenna,Goyal Neelam,Sakamuri Sarada,So Yuen T.,Paulose Shirley,Pol Sabrina,Welsh Lesly,Bhavaraju-Sanka Ratna,Tobon Gonzales Alejandro,Dishman Lorraine,Jones Floyd,Gonzalez Anna,Padilla Patricia,Saklad Amy,Silva Marcela,Nations Sharon,Trivedi Jaya,Hopkins Steve,Kazamel Mohamed,Alsharabati Mohammad,Lu Liang,Nozaki Kenkichi,Mumfrey-Thomas Sandi,Woodall Amy,Mozaffar Tahseen,Cash Tiyonnoh,Goyal Namita,Roy Gulmohor,Mathew Veena,Maqsood Fatima,Minton Brian,Jones H. James,Rosenfeld Jeffrey,Garcia Rebekah,Echevarria Laura,Garcia Sonia,Pulley Michael,Aranke Shachie,Berger Alan Ross,Shah Jaimin,Shabbir Yasmeen,Smith Lisa,Varghese Mary,Gutmann Laurie,Gutmann Ludwig,Jerath Nivedita,Nance Christopher,Swenson Andrea,Olalde Heena,Kressin Nicole,Sieren Jeri,Dimachkie Mazen,Glenn Melanie,McVey April,Pasnoor Mamatha,Statland Jeffery,Wang Yunxia,Liu Tina,Emmons Kelley,Jenci Nicole,Locheke Jerry,Fondaw Alex,Johns Kathryn,Rico Gabrielle,Walsh Maureen,Herbelin Laura,Hafer-Macko Charlene,Kwan Justin,Zilliox Lindsay,Callison Karen,Young Valerie,DiSanzo Beth,Naunton Kerry,Bilsker Martin,Sharma Khema,Cooley Anne,Reyes Eliana,Michon Sara-Claude,Sheldon Danielle,Steele Julie,Karam Chafic,Chopra Manisha,Traub Rebecca,Katzin Lara,McClain Terry,Harvey Brittany,Hart Adam,Huynh Kristin,Beydoun Said,Chilingaryan Amaiak,Doan Victor,Droker Brian,Gong Hui,Karimi Sanaz,Lin Frank,McClain Terry,Pokala Krishna,Shah Akshay,Tran Anh,Akhter Salma,Malekniazi Ali,Tandan Rup,Hehir Michael,Waheed Waqar,Lucy Shannon,Weiss Michael,Distad Jane,Strom Susan,Downing Sharon,Kim Bryan,Bertorini Tulio,Arnold Thomas,Hendersen Kendrick,Pillai Rekha,Liu Ye,Wheeler Lauren,Hewlett Jasmine,Vanderhook Mollie,Dicapua Daniel,Keung Benison,Kumar Aditya,Patwa Huned,Robeson Kimberly,Yang Irene,Nye Joan,Vu Hong,

Affiliation:

1. Department of Neurology and NeurosciencesStanford University School of Medicine Stanford California USA

2. Department of NeurologyHanamaki General Hospital Hanamaki Japan

3. Department of NeurologyUniversity of Miami Miller School of Medicine Miami Florida USA

4. Department of NeurologyInternational University of Health and Welfare Narita Japan

5. Department of NeurologyUniversity of Kansas Medical Center Kansas City Kansas USA

6. Neurology Department, Hospital Sant PauAutonomous University of Barcelona Barcelona Spain

7. Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER) Spain

8. Queen Elizabeth Neuroscience Centre and Wellcome Trust Clinical Research FacilityUniversity Hospital Birmingham Birmingham United Kingdom

9. Department of Neurology, RigshospitaletUniversity of Copenhagen Copenhagen Denmark

10. Department of NeurologyUniversity of Virginia Health System Charlottesville Virginia USA

11. Department of NeurologyThe Ohio State University Columbus Ohio USA

12. Department of Neurology, Yale School of MedicineYale University New Haven Connecticut USA

13. Department of NeurologyAarhus University Hospital Aarhus Denmark

14. Department of NeurologyBellvitge University Hospital Barcelona Spain

15. Neuromuscular Reference CentreGhent University Hospital Ghent Belgium

16. Department of NeurologyUniversity of South Florida Tampa Florida USA

17. Foundation of the Carlo Besta Neurological InstituteIRCSS Milan Italy

18. Alexion Pharmaceuticals Boston Massachusetts USA

19. Department of NeurologyUniversity of North Carolina Chapel Hill North Carolina USA

Funder

Alexion Pharmaceuticals

Publisher

Wiley

Subject

Physiology (medical),Cellular and Molecular Neuroscience,Neurology (clinical),Physiology

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