Transatlantic progress in measurement of cognitive outcomes in paediatric oncology trials

Author:

Thomas Sophie12ORCID,Embry Leanne3,Walsh Karin45ORCID,Bull Kim6,Grundy Richard12,Kennedy Colin6,Lemiere Jurgen7,Hernáiz Driever Pablo8ORCID,Limond Jennifer9,Chevignard Mathilde101112,Hardy Kristina45

Affiliation:

1. Department of Paediatric Neuropsychology Nottingham Children's Hospital, Queen's Medical Centre Nottingham UK

2. Child Brain Tumour Research Centre, School of Medicine, Queen's Medical Centre University of Nottingham Nottingham UK

3. Pediatric Hematology/Oncology UT Health San Antonio Texas USA

4. Division of Pediatric Neuropsychology Children's National Hospital Washington, DC USA

5. Departments of Psychiatry & Behavioral Medicine and Pediatrics, The George Washington University School of Medicine Washington, DC USA

6. Clinical and Experimental Sciences, Faculty of Medicine University of Southampton Southampton General Hospital UK

7. Department Oncology, Pediatric Hemato‐Oncology, KULeuven University Hospital Leuven Leuven Belgium

8. Department of Pediatric Oncology and Hematology, Berlin Institute of Health Charité‐Universitätsmedizin Berlin Humboldt‐Universität zu Berlin, Berlin Germany

9. Department of Psychology University of Exeter Exeter UK

10. Rehabilitation Department for Children with Acquired Neurological Injury; and Outreach Team for Children and Adolescents with Acquired Brain Injury Saint Maurice Hospitals Saint Maurice France

11. Laboratoire d'Imagerie Biomédicale, LIB Sorbonne Université Paris France

12. GRC24 Handicap Moteur et Cognitif et Réadaptation (HaMCRe) Sorbonne Université Paris France

Abstract

AbstractThe importance of measuring quality of survival within paediatric oncology trials is increasingly recognised. However, capturing neuropsychological outcomes and other aspects of quality of survival in the context of large or multinational trials can be challenging. We provide examples of protocols designed to address this challenge recently employed in clinical trials in the USA and Europe. We discuss their respective strengths and challenges, obstacles encountered and future opportunities for transatlantic collaboration.

Publisher

Wiley

Subject

Oncology,Hematology,Pediatrics, Perinatology and Child Health

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