Drug repositioning screening identifies etravirine as a potential therapeutic for friedreich's ataxia

Author:

Alfedi Giulia1,Luffarelli Riccardo1,Condò Ivano1,Pedini Giorgia2,Mannucci Liliana2,Massaro Damiano S.1,Benini Monica13,Toschi Nicola45,Alaimo Giorgia13,Panarello Luca1,Pacini Laura2,Fortuni Silvia1,Serio Dario1,Malisan Florence1,Testi Roberto13,Rufini Alessandra13ORCID

Affiliation:

1. Laboratory of Signal Transduction, Department of Biomedicine and Prevention; University of Rome “Tor Vergata”; Rome Italy

2. Laboratory of Molecular Neurobiology, Department of Biomedicine and Prevention; University of Rome “Tor Vergata”; Rome Italy

3. Fratagene Therapeutics Srl; Rome Italy

4. Medical Physics Section, Department of Biomedicine and Prevention; University of Rome “Tor Vergata”; Rome Italy

5. Department of Radiology; Athinoula A. Martinos Center for Biomedical Imaging and Harvard Medical School; Boston Massachusetts USA

Funder

H2020 European Research Council

Fondazione Telethon

National Ataxia Foundation

University of Rome Tor Vergata - Mission Sustainability

Publisher

Wiley

Subject

Clinical Neurology,Neurology

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