Hematopoietic stem cell transplantation for Gaucher disease

Author:

Somaraju Usha Rani R1,Tadepalli Krishna2

Affiliation:

1. Star Hospitals; Hyderabad India

2. SK Diagnostics; Hyderabad India

Publisher

Wiley

Subject

Pharmacology (medical)

Reference80 articles.

1. Pharmacokinetics of Novel Plant Cell-Expressed Taliglucerase Alfa in Adult and Pediatric Patients with Gaucher Disease;Abbas;PLoS ONE [electronic Resource],2015

2. Almon E Novel enzyme replacement therapy for Gaucher disease; on-going phase 3 clinical trial with recombinant human glucocerebrosidase expressed in plant cells Proceedings of the 8th European Working Group on Gaucher Disease (EWGGD); 2008 June 4-7; Budapest, Hungary 2008 18

3. Baker KS Study of pulmonary complications in Pediatric Patients With Storage Disorders undergoing Allogeneic Hematopoietic stem cell transplantation www.clinicaltrials.gov

4. Barranger J Phase I study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene into peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher disease www.clinicaltrials.gov

5. EDGE: A Phase 3 study evaluating once versus twice daily dosing of eliglustat in patients with Gaucher disease type 1: Interim results from the lead-in-period;Charrow;Molecular Genetics and Metabolism,2014

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