Are rare diseases still orphans or happily adopted? The challenges of developing and using orphan medicinal products-Reference-Cited by-全球学者库

Are rare diseases still orphans or happily adopted? The challenges of developing and using orphan medicinal products

Published:2006-09 Issue:3 Volume:62 Page:264-271
ISSN:0306-5251
Container-title:British Journal of Clinical Pharmacology
language:en
Short-container-title:Br J Clin Pharmacol

Author:

Dear James W.,Lilitkarntakul Pajaree,Webb David J.

Publisher

Wiley

Subject

Pharmacology (medical),Pharmacology

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/j.1365-2125.2006.02654.x/fullpdf

Reference27 articles.

1. Adopting an orphan

2. 2 Orphan Drug Act. http://www.fda.gov/orphan/oda.htm2005 Last accessed 13 December 2005.

3. 3 European Committee for Orphan Medicinal Products. http://www.emea.eu.International/htms/general/contacts/COMP.html2005 Last accessed 13 December 2005.

4. 4 Regulation (EC) no. 141/2000 of the European Parliament and the Council of 16 December 1999 on Orphan Medicinal Products. http://europa.eu.int/eur-lex/lex/LexUriServ/LexUriServ.do?uri=CELEX.32000R0141:EN.HTML 2005 Last accessed 13 December 2005.

5. 5 Loughnot D. Potential interactions of the Orphan Drug Act and pharmacogenomics: a flood of orphan drugs and abuses? Am J Law Med 2005; 31: 365-80.

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