A compilation of national plans, policies and government actions for rare diseases in 23 countries
Author:
Affiliation:
1. Division of Human Development and Disability, National Center on Birth Defects and Developmental Disabilities, Centers for Disease Control and Prevention
Publisher
International Research and Cooperation Association for Bio & Socio-Sciences Advancement (IRCA-BSSA)
Subject
General Medicine
Link
https://www.jstage.jst.go.jp/article/irdr/7/4/7_2018.01085/_pdf
Reference71 articles.
1. 1. Gammie T, Lu CY, Babar ZU. Access to Orphan Drugs: A Comprehensive Review of Legislations, Regulations and Policies in 35 Countries. PLoS One. 2015; 10:e0140002.
2. 2. Franco P. Orphan drugs: the regulatory environment. Drug Discov Today. 2013; 18:163-172.
3. 3. van Weely S, Leufkens HGM. World Health Organization. Update on 2004 Background Paper, BP 6.19 Rare Diseases. http://www.who.int/medicines/areas/priority_medicines/BP6_19Rare.pdf (accessed July 27, 2018).
4. 4. Eurordis. About Rare Diseases. https://www.eurordis.org/about-rare-diseases (accessed July 27, 2018).
5. 5. Forman J, Taruscio D, Llera VA, Barrera LA, Coté TR, Edfjäll C, Gavhed D, Haffner ME, Nishimura Y, Posada M, Tambuyzer E, Groft SC, Henter JI; International Conference for Rare Diseases and Orphan Drugs (ICORD). The need for worldwide policy and action plans for rare diseases. Acta Paediatr. 2012; 101:805-807.
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