Vosoritide, a miracle drug, covering unmet need in achondroplasia: A regulatory update-Reference-Cited by-同舟云学术

Vosoritide, a miracle drug, covering unmet need in achondroplasia: A regulatory update

Published:2023-11-30 Issue:4 Volume:12 Page:257-261
ISSN:2186-361X
Container-title:Intractable & Rare Diseases Research
language:en
Short-container-title:IRDR

Author:

Simran ¹,Devi S S Kirthiga¹,Chetan Dushantrao Sabanis¹,Joga Ramesh¹,Kumar Sandeep¹

Affiliation:

1. Department of Regulatory Affairs, National Institute of Pharmaceutical Education and Research (NIPER), Hyderabad, India.

Publisher

International Research and Cooperation Association for Bio & Socio-Sciences Advancement (IRCA-BSSA)

Subject

General Medicine

Link

https://www.jstage.jst.go.jp/article/irdr/12/4/12_2023.01055/_pdf

Reference22 articles.

1. 1. Ministry of Health and Family Welfare. National policy for rare diseases, 2021. https://main.mohfw.gov.in/sites/default/files/Final%20NPRD%2C%202021.pdf (accessd February 11, 2023).

2. 2. National Institute of Health. Achondroplasia. https://rarediseases.info.nih.gov/diseases/8173/achondroplasia#:~:text=Achondroplasia%20is%20a%20disorder%20of,small%20fingers%2C%20and%20normal%20intelligence (accessd February 8, 2023).

3. 3. Baujat G, Legeai-Mallet L, Finidori G, Cormier-Daire V, Le Merrer M. Achondroplasia. Best Prac & Res Clin Rheum. 2008; 22:3-18.

4. 4. MedlinePlus. FGFR3 gene. https://medlineplus.gov/genetics/gene/fgfr3/#conditions (accessd February 27, 2023).

5. 5. Horton WA, Hall JG, Hecht JT. Achondroplasia. Lancet. 2007; 370:162-172.

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