Innovation for rare diseases and bioethical concerns: A thin thread between medical progress and suffering
Author:
Publisher
Baishideng Publishing Group Inc.
Subject
Pediatrics, Perinatology and Child Health
Reference52 articles.
1. Compounded medication for patients with rare diseases
2. Challenges of developing and conducting clinical trials in rare disorders
3. Failures to further developing orphan medicinal products after designation granted in Europe: an analysis of marketing authorisation failures and abandoned drugs
4. Germ-free delivery. The initiation of management of infants with a high probability of congenital immune deficiency states
5. Bealmear PM, South MA, Wilson R. David’s story: the gift of 12 years, 5 months, and 1 day. Prog Clin Biol Res 1985; 181: 475-489
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