Effectiveness of lumacaftor/ivacaftor initiation in children with cystic fibrosis aged 2 through 5 years on disease progression: Interim results from an ongoing registry-based study

Author:

Kim ClaireORCID,Higgins Mark,Liu Lingyun,Volkova Nataliya,Zolin AnnaORCID,Naehrlich LutzORCID,Andreas Pfleger (AT),Elise Lammertijn (BE),Duška Tješić-Drinković (HR),Pavel Dřevínek (CZ),Milan Macek,Hanne Vebert Olesen (DK),Nathalie Senecal (FR),Pierre-Régis Burgel (FR),Godfrey Fletcher (IE),Rita Padoan (IT),Annalisa Orenti (IT),Federico Ambrogi (IT),Simone Gambazza (IT),Elīna Aleksejeva (LV),Anna-Maria Charatsi (LU),Domenique Zomer (NL),Egil Bakkeheim (NO),Lukasz Woźniacki (PL),Uroš Krivec (SI),Christina Krantz (SE),Anders Lindblad (SE),Andreas Jung (CH),Sarah Clarke (UK),Siobhán B․ Carr (UK)

Funder

Vertex Pharmaceuticals Incorporated

Publisher

Elsevier BV

Reference19 articles.

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