1. Design of sample surveys to estimate the prevalence of rare diseases: three unbiased estimates;Birnbaum;Vital-Health-Stat-1,1965
2. Nieuwe geneesmiddelen voor zeldzame ziekten;Baruch;Tijdschr-Ziekenverpl,1966
3. Orphan drugs –debunking a myth;Althuis;N Engl J Med,1980
4. Commission report Part I: introduction;J Rare Disease,1996
5. The Orphan Drug Act. Public Law 97-414 January 4, 1983