Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen-Reference-Cited by-同舟云学术

Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen

Published:2021-07 Issue:7 Volume:31 Page:596-602
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Coratti Giorgia,Pane Marika,Lucibello Simona,Pera Maria Carmela,Pasternak Amy,Montes Jacqueline,Sansone Valeria A,Duong Tina,Dunaway Young Sally,Messina Sonia,D'Amico Adele,Civitello Matthew,Glanzman Allan M,Bruno Claudio,Salmin Francesca,Tacchetti Paola,Carnicella Sara,Sframeli Maria,Antonaci Laura,Frongia Anna Lia,De Vivo Darryl C.,Darras Basil T.,Day John,Bertini Enrico,Muntoni Francesco,Finkel Richard,Mercuri Eugenio

Funder

Spinal Muscular Atrophy Foundation

Biogen Inc

Telethon Italy

Publisher

Elsevier BV

Subject

Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health

Reference26 articles.

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