Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease-Reference-Cited by-同舟云学术

Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease

Published:2018-02 Issue: Volume:68 Page:203-208
ISSN:1079-9796
Container-title:Blood Cells, Molecules, and Diseases
language:en
Short-container-title:Blood Cells, Molecules, and Diseases

Author:

Biegstraaten M.,Cox T.M.,Belmatoug N.,Berger M.G.,Collin-Histed T.^ORCID,Vom Dahl S.,Di Rocco M.,Fraga C.,Giona F.,Giraldo P.,Hasanhodzic M.^ORCID,Hughes D.A.,Iversen P.O.,Kiewiet A.I.,Lukina E.,Machaczka M.,Marinakis T.,Mengel E.,Pastores G.M.,Plöckinger U.,Rosenbaum H.,Serratrice C.,Symeonidis A.,Szer J.,Timmerman J.,Tylki-Szymańska A.,Weisz Hubshman M.,Zafeiriou D.I.,Zimran A.,Hollak C.E.M.

Funder

The Netherlands Organisation for Health Research and Development

Publisher

Elsevier BV

Subject

Cell Biology,Hematology,Molecular Biology,Molecular Medicine

Reference30 articles.

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5. Phase 1/2 and extension study of velaglucerase alfa replacement therapy in adults with type 1 Gaucher disease: 48-month experience;Zimran;Blood,2010

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