Immunogenicity to cerliponase alfa intracerebroventricular enzyme replacement therapy for CLN2 disease: Results from a Phase 1/2 study-Reference-Cited by-同舟云学术

Immunogenicity to cerliponase alfa intracerebroventricular enzyme replacement therapy for CLN2 disease: Results from a Phase 1/2 study

Published:2018-12 Issue: Volume:197 Page:68-76
ISSN:1521-6616
Container-title:Clinical Immunology
language:en
Short-container-title:Clinical Immunology

Author:

Cherukuri Anu,Cahan Heather,de Hart Greg,Van Tuyl Andrea^ORCID,Slasor Peter,Bray Laurie,Henshaw Joshua,Ajayi Temitayo,Jacoby Dave,O'Neill Charles A.,Schweighardt Becky

Funder

BioMarin Pharmaceutical, Inc.

Publisher

Elsevier BV

Subject

Immunology,Immunology and Allergy

Reference46 articles.

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4. Moving towards effective therapeutic strategies for neuronal ceroid lipofuscinosis;Geraets;Orphanet J. Rare Dis.,2016

5. CLN2 disease;Kohlschütter;Pediatr. Endocrinol. Rev.,2016

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