Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results-Reference-Cited by-同舟云学术

Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results

Published:2019-01 Issue: Volume:197 Page:65-73
ISSN:0002-9394
Container-title:American Journal of Ophthalmology
language:en
Short-container-title:American Journal of Ophthalmology

Author:

Lam Byron L.,Davis Janet L.,Gregori Ninel Z.,MacLaren Robert E.,Girach Aniz,Verriotto Jennifer D.,Rodriguez Belen,Rosa Potyra R.,Zhang Xiaojun,Feuer William J.

Funder

Hope for Vision Arsht Fund

Bascom Palmer Eye Institute

University of Miami

Miller School of Medicine

National Eye Institute

Publisher

Elsevier BV

Subject

Ophthalmology

Reference20 articles.

1. Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial;MacLaren;Lancet,2014

2. Choroideremia: a review of general findings and pathogenesis;Coussa;Ophthalmic Genet,2012

3. Remodeling of the human retina in choroideremia: rab escort protein 1 (REP-1) mutations;Jacobson;Invest Ophthalmol Vis Sci,2006

4. High-resolution images of retinal structure in patients with choroideremia;Syed;Invest Ophthalmol Vis Sci,2013

5. Pathogenic mechanisms and the prospect of gene therapy for choroideremia;Dimopoulos;Expert Opin Orphan Drugs,2015

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