Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice-Reference-Cited by-同舟云学术

Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice

Published:2018-02 Issue:2 Volume:26 Page:496-509
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bunting Stuart,Zhang Lening,Xie Lin,Bullens Sherry,Mahimkar Rajeev,Fong Sylvia,Sandza Krystal,Harmon Danielle,Yates Bridget,Handyside Britta,Sihn Choong-Ryoul,Galicia Nicole,Tsuruda Laurie,O’Neill Charles A.,Bagri Anil,Colosi Peter,Long Shinong,Vehar Gordon,Carter Barrie

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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