Cochlear transduction via cerebrospinal fluid delivery of AAV in non-human primates
Author:
Funder
NIH
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference20 articles.
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3. Targeting the lung epithelium after intravenous delivery by directed evolution of underexplored sites on the AAV capsid;Goertsen;Mol. Ther. Methods Clin. Dev.,2022
4. Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editing;Gonzalez;Nat. Commun.,2022
5. A systematic capsid evolution approach performed in vivo for the design of AAV vectors with tailored properties and tropism;Davidsson;Proc. Natl. Acad. Sci. USA,2019
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3. Human cochlear diffusion from the cerebrospinal fluid space with gadolinium contrast;Molecular Therapy;2023-09
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