Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil-Reference-Cited by-同舟云学术

Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil

Published:2021-07 Issue:7 Volume:29 Page:2378-2386
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Giugliani Roberto,Martins Ana Maria,So Sairei,Yamamoto Tatsuyoshi,Yamaoka Mariko,Ikeda Toshiaki,Tanizawa Kazunori,Sonoda Hiroyuki,Schmidt Mathias,Sato Yuji^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference29 articles.

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3. Neurological manifestations of lysosomal disorders and emerging therapies targeting the CNS;Giugliani;Lancet Child Adolesc. Health,2018

4. Novel Enzyme Replacement Therapies for Neuropathic Mucopolysaccharidoses;Sato;Int. J. Mol. Sci.,2020

5. A phase II/III clinical study of enzyme replacement therapy with idursulfase in mucopolysaccharidosis II (Hunter syndrome);Muenzer;Genet. Med.,2006

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