5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency-Reference-Cited by-同舟云学术

5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency

Published:2017-06 Issue:6 Volume:25 Page:1387-1394
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Mueller Christian,Gernoux Gwladys,Gruntman Alisha M.,Borel Florie,Reeves Emer P.,Calcedo Roberto,Rouhani Farshid N.,Yachnis Anthony,Humphries Margaret,Campbell-Thompson Martha,Messina Louis,Chulay Jeffrey D.,Trapnell Bruce,Wilson James M.,McElvaney Noel G.,Flotte Terence R.

Funder

NHLBI and NIDDK of the NIH

Office of Orphan Products Development, United States Food and Drug Administration

AGTC

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference24 articles.

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2. Natural history and life expectancy in severe alpha1-antitrypsin deficiency, Pi Z;Larsson;Acta Med. Scand.,1978

3. Alpha 1-antitrypsin deficiency deaths in the United States from 1979-1991. An analysis using multiple-cause mortality data;Browne;Chest,1996