Measurements of Functional Responses in Human Primary Lung Cells as a Basis for Personalized Therapy for Cystic Fibrosis

Author:

Awatade Nikhil T.,Uliyakina Inna,Farinha Carlos M.,Clarke Luka A.,Mendes Karina,Solé Amparo,Pastor Juan,Ramos Maria MargaridaORCID,Amaral Margarida D.ORCID

Funder

POCTI/FCT/PIDDAC

FCT, Portugal

Gilead GÉNESE Programme

Publisher

Elsevier BV

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Reference24 articles.

1. CFTR and chaperones: processing and degradation;Amaral;J. Mol. Neurosci.,2004

2. Rescuing mutant CFTR: a multi-task approach to a better outcome in treating cystic fibrosis;Amaral;Curr. Pharm. Des.,2013

3. New pharmacological approaches for cystic fibrosis: promises, progress, pitfalls;Bell;Pharmacol. Ther.,2015

4. Cystic fibrosis: a worldwide analysis of CFTR mutations—correlation with incidence data and application to screening;Bobadilla;Hum. Mutat.,2002

5. ivacaftor, a CFTR potentiator, in cystic fibrosis patients who have a non-G551D-CFTR gating mutation: phase 3, part 1 results;De Boeck;Pediatr. Pulmonol.,2013

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