Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial
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Published:2023-11
Issue:
Volume:65
Page:102258
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ISSN:2589-5370
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Container-title:eClinicalMedicine
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language:en
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Short-container-title:eClinicalMedicine
Author:
Savarirayan RaviORCID,
Hoernschemeyer Daniel G.,
Ljungberg Merete,
Zarate Yuri A.,
Bacino Carlos A.,
Bober Michael B.,
Legare Janet M.,
Högler Wolfgang,
Quattrin Teresa,
Abuzzahab M. Jennifer,
Hofman Paul L.,
White Klane K.,
Ma Nina S.,
Schnabel Dirk,
Sousa Sérgio B.,
Mao Meng,
Smith Alden,
Chakraborty Mukta,
Giwa Adebola,
Winding Bent,
Volck Birgitte,
Shu Aimee D.,
McDonnell CiaraORCID