Efficacy and safety of pegzilarginase in arginase 1 deficiency (PEACE): a phase 3, randomized, double-blind, placebo-controlled, multi-centre trial
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Published:2024-02
Issue:
Volume:68
Page:102405
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ISSN:2589-5370
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Container-title:eClinicalMedicine
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language:en
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Short-container-title:eClinicalMedicine
Author:
Russo Rossana SanchezORCID,
Gasperini Serena,
Bubb Gillian,
Neuman LindaORCID,
Sloan Leslie S.,
Diaz George A.,
Enns Gregory M.
Funder
Aeglea BioTherapeutics
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5. Clinical features and neurologic progression of hyperargininemia;Carvalho;Pediatr Neurol,2012