Effects of tofersen treatment in patients with SOD1-ALS in a “real-world” setting – a 12-month multicenter cohort study from the German early access program-Reference-Cited by-同舟云学术

Effects of tofersen treatment in patients with SOD1-ALS in a “real-world” setting – a 12-month multicenter cohort study from the German early access program

Published:2024-03 Issue: Volume:69 Page:102495
ISSN:2589-5370
Container-title:eClinicalMedicine
language:en
Short-container-title:eClinicalMedicine

Author:

Wiesenfarth Maximilian^ORCID,Dorst Johannes,Brenner David,Elmas Zeynep,Parlak Özlem,Uzelac Zeljko,Kandler Katharina,Mayer Kristina,Weiland Ulrike,Herrmann Christine,Schuster Joachim,Freischmidt Axel,Müller Kathrin,Siebert Reiner,Bachhuber Franziska,Simak Tatiana,Günther Kornelia^ORCID,Fröhlich Elke,Knehr Antje,Regensburger Martin^ORCID,German Alexander,Petri Susanne,Grosskreutz Julian^ORCID,Klopstock Thomas,Reilich Peter^ORCID,Schöberl Florian,Hagenacker Tim,Weyen Ute,Günther René,Vidovic Maximilian^ORCID,Jentsch Martin,Haarmeier Thomas,Weydt Patrick,Valkadinov Ivan,Hesebeck-Brinckmann Jasper^ORCID,Conrad Julian,Weishaupt Jochen Hans,Schumann Peggy,Körtvélyessy Peter,Meyer Thomas,Ruf Wolfgang Philipp^ORCID,Witzel Simon,Senel Makbule,Tumani Hayrettin,Ludolph Albert Christian

Publisher

Elsevier BV

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2. Clinical characterization of common pathogenic variants of SOD1-ALS in Germany;Journal of Neurology;2024-08-14

3. Changes in Cerebrospinal Fluid Concentrations of Selenium Species Induced by Tofersen Administration in Subjects with Amyotrophic Lateral Sclerosis Carrying SOD1 Gene Mutations;Biological Trace Element Research;2024-07-17

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5. Clinical and patient‐reported outcomes and neurofilament response during tofersen treatment in SOD1‐related ALS—A multicenter observational study over 18 months;Muscle & Nerve;2024-06-20