1. O. of the Commissioner: Press Announcements – FDA Approves Novel Gene Therapy to Treat Patients with a Rare form of Inherited Vision Loss. [Online]. Available: https://www.fda.gov/newsevents/newsroom/pressannouncements/ucm589467.htm. (Accessed 26 July 2018).
2. Mendell JR et al.: Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy. https://doi.org/10.1056/NEJMoa1706198, 01-Nov-2017. [Online]. Available: https://www.nejm.org/doi/10.1056/NEJMoa1706198?url_ver=Z39.88-2003&rfr_id=ori%3Arid%3Acrossref.org&rfr_dat=cr_pub%3Dwww.ncbi.nlm.nih.gov. (Accessed 6 September 2018).
3. Hemophilia gene therapy comes of age;George;Blood Adv,2017
4. Fields’ Virology;Knipe,2007
5. Adeno-associated virus antibody profiles in newborns, children, and adolescents;Calcedo;Clin Vaccine Immunol,2011